Zolgensma, an FDA approved gene therapy, supplements the production of the SMN protein to improve motor neuron function in children with spinal muscular atrophy after just one dose.
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Researchers report people with higher empathy process music with greater involvement in the brain's reward system and areas of the brain associated with social information processing.
WUSTL researchers have converted skin cells into motor neurons without going through the stem cell state. The new technique could help in the development of devastating neurodegenerative diseases, like ALS, that affect motor neurons.
Researchers report a synthetic molecule can reduce tau and even reverse some neurological damage in mouse models of Alzheimer's disease.
A new study implicates a key cellular mechanism as defective in SMA for the first time, providing a new lead for developing future interventions.