Zolgensma, an FDA approved gene therapy, supplements the production of the SMN protein to improve motor neuron function in children with spinal muscular atrophy after just one dose.
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Researchers report people with higher empathy process music with greater involvement in the brain's reward system and areas of the brain associated with social information processing.
Targeting autophagy may help in the battle against ALS and other diseases that affect motor neurons, researchers report.
WUSTL researchers have converted skin cells into motor neurons without going through the stem cell state. The new technique could help in the development of devastating neurodegenerative diseases, like ALS, that affect motor neurons.
Researchers implicate a variant in the UBQLN4 gene as a possible cause of ALS. The variant disrupts cellular processes that drive motor neuron development.
Researchers have identified a compound that can stabilize a protein implicated in ALS and SMN.
Researchers report a synthetic molecule can reduce tau and even reverse some neurological damage in mouse models of Alzheimer's disease.
A new study reports on how our brain decides if performing a certain task is worth the effort.
Researchers believe they have discovered a promising new treatment for spinal muscular atrophy, a leading genetic cause of death in children.
Researchers have identified how specific brain areas change over time in patients with Parkinson's disease.
A new drug shows promise for improving outcomes for people with SMA.
A new study implicates a key cellular mechanism as defective in SMA for the first time, providing a new lead for developing future interventions.
