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gene therapy

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Featured Genetics Neurology

·July 29, 2020·6 min read

Getting Gene Therapy to the Brain

Researchers successfully applied a gene therapy platform to completely correct brain defects in a large animal model of a human genetic disease.

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Featured Genetics Neuroscience Open Neuroscience Articles Visual Neuroscience

·May 1, 2020·5 min read

New gene therapy for complete color blindness tested in patients

New gene therapy may help those with achromatopsia, or complete color blindness, to improve visual function. The treatment targets the CNGA3 gene, which is implicated in one-third of achromatopsia cases.

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Featured Genetics Neurology Neuroscience Open Neuroscience Articles

·January 3, 2020·2 min read

Using gene therapy to treat CTE

A newly developed adeno-associated virus vector can deliver an anti-p Tau antibody directly to the hippocampus, significantly reducing pTau levels associated with CTE.

This shows the retina with and without gene therapy

Featured Genetics Neuroscience Visual Neuroscience

·July 8, 2019·3 min read

Retina restructures itself after cell death

Gene therapy can restore the structure of the retina and regain normal light responses.

This shows baby Arabella Smygov following gene therapy treatment for SMA

Featured Genetics Neurology Neuroscience

·June 10, 2019·7 min read

‘Like Looking at a Miracle’: Baby Blossoms Thanks to Gene Therapy For Spinal Muscular Atrophy

Zolgensma, an FDA approved gene therapy, supplements the production of the SMN protein to improve motor neuron function in children with spinal muscular atrophy after just one dose.

dna

Featured Genetics Neurology Neuroscience Open Neuroscience Articles

·January 19, 2019·3 min read

Gene Therapy Promotes Nerve Regeneration

A new study reveals gene therapy in combination with neurosurgery can help to improve the rate of survival and promote regeneration of nerve fibers.

Image shows a Toxoplasma tissue cyst.

Featured Neurology Neuroscience

·June 19, 2017·6 min read

How to Stop the Nasty Lurking Toxoplasmosis Parasite? Target Its ‘Stomach’

Study suggests new avenues for treating toxoplasmosis parasite infections.

Image shows the cochlear.

Auditory Neuroscience Featured Genetics Neuroscience Open Neuroscience Articles

·April 11, 2017·5 min read

Success of Sensory Cell Regeneration Raises Hope for Hearing Restoration

By manipulating two genes, researchers have been able to regenerate immature auditory hair cells.

Brain Cancer Featured Genetics Neurology Open Neuroscience Articles

·January 4, 2017·5 min read

Immunotherapy and Gene Therapy Combinations Show Promise Against Glioblastoma

Researchers suggest using both immunotherapy and gene therapy to help patients fight against glioblastoma brain cancer.

Image shows brain cells from a mouse cortex.

Featured Genetics Neurology Open Neuroscience Articles

·October 10, 2016·6 min read

Alzheimer’s Could be Treated With Gene Therapy: Mouse Study

Researchers report they have successfully prevented the development of Alzheimer's in mice by using gene therapy delivered by a virus to the brain.

Image shows a brain slice from a huntington's patient.

Featured Genetics Neurology Open Neuroscience Articles

·September 9, 2016·5 min read

Activity of Huntington’s Disease Gene Curbed for 6 Months: Mouse Study

Researchers have identified a protein that can turn off the Huntingtin gene's expression.

Image shows a hippocampal slice.

Featured Genetics

·December 9, 2015·4 min read

Gene Therapy Could Extend Estrogen’s Protective Effects on Memory

Researchers use gene therapy to help extend the effectiveness of estrogen for retaining memory.

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