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gene therapy

Featured Genetics Neurology Open Neuroscience Articles

·March 19, 2021·3 min read

Gene Therapy Using ‘Zinc Fingers’ May Help Treat Alzheimer’s Disease

A new genetic engineering strategy significantly reduces levels of tau in animal models of Alzheimer's disease. The treatment, which involves a single injection, appears to have long-last effects.

Featured Genetics Neuroscience Open Neuroscience Articles Visual Neuroscience

·October 10, 2022·4 min read

Gene Therapy Rapidly Improves Night Vision in Adults With Congenital Blindness

Gene therapy enables a striking recovery of night vision in those who suffer from the childhood-onset blindness disorder Leber Congenital Amaurosis.

Featured Neuroscience

·October 10, 2024·5 min read

Controlling Brain Activity with Magnetic Fields

Researchers have developed a breakthrough technology using magnetic fields to control specific brain circuits non-invasively, potentially transforming treatments for conditions like Parkinson’s and depression. This technique, termed "magnetogenetics," delivers gene therapy to target neurons and uses magnetic fields to activate or inhibit them, allowing precise manipulation without invasive implants. In mouse studies, this approach successfully reduced movement issues associated with Parkinson’s. Future research aims to explore clinical applications for psychiatric disorders and chronic pain, providing a new frontier in brain circuit modulation.

Featured Genetics

·December 9, 2015·4 min read

Gene Therapy Could Extend Estrogen’s Protective Effects on Memory

Researchers use gene therapy to help extend the effectiveness of estrogen for retaining memory.

Events Featured Genetics

·May 24, 2012·4 min read

Workshop to Examine Optogenetic Approaches for Treating Diseases Associated With Vision Loss Announced

Foundation Fighting Blindness and Mass. Eye and Ear Host June 1 Optogenetics Workshop to Fast-Track Innovative Approaches to Save and...

Featured Genetics Neuroscience

·July 3, 2023·6 min read

AI Predicts CRISPR’s RNA-Targeting Effects, Revolutionizing Gene Therapy

Researchers developed a deep learning model, TIGER, that accurately predicts on- and off-target activity of RNA-targeting CRISPR tools. This new approach allows the fine-tuning of gene activity in human cells.

Image shows a brain slice from a huntington's patient.

Featured Genetics Neurology Open Neuroscience Articles

·September 9, 2016·5 min read

Activity of Huntington’s Disease Gene Curbed for 6 Months: Mouse Study

Researchers have identified a protein that can turn off the Huntingtin gene's expression.

Featured Genetics Neurology

·July 29, 2020·6 min read

Getting Gene Therapy to the Brain

Researchers successfully applied a gene therapy platform to completely correct brain defects in a large animal model of a human genetic disease.

Featured Genetics Neurology Neuroscience

·May 7, 2026·7 min read

Gene Therapy Restores Walking After Paralysis

Researchers have used a designer cytokine, hIL-6, to "rewire" the spinal cord by stimulating the sprouting of new connections from intact nerve fibers. This approach successfully restored coordinated walking in paralyzed mice, highlighting a powerful new strategy for treating spinal cord contusions.

Featured Genetics Neurology Neuroscience

·May 9, 2022·4 min read

Gene Therapy Shows Promise in Treating Neuropathy From Spinal Cord Injuries

Gene therapy that inhibits targeted nerve cell signals effectively improves symptoms of neuropathic pain without negative side effects in mouse models of spinal cord injury or peripheral nerve damage.

Featured Genetics Neuroscience Visual Neuroscience

·August 23, 2022·4 min read

Gene Therapy for Completely Color Blind Children Partly Restores Cone Function

Researchers partially restored the function of cone receptors in the retinas of children born completely blind by using gene therapy.

Featured Genetics Neurology Neuroscience

·May 26, 2026·10 min read

Gene Therapy Proven to Shield Brain from TDP-43 Damage

An experimental gene therapy called SynCav1 can protect the central nervous system from the cognitive decline linked to TDP-43-related proteinopathy, a primary driver of FTD, ALS, and over half of all Alzheimer’s cases.

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gene therapy

Gene Therapy Using ‘Zinc Fingers’ May Help Treat Alzheimer’s Disease

Gene Therapy Rapidly Improves Night Vision in Adults With Congenital Blindness

Controlling Brain Activity with Magnetic Fields

Gene Therapy Could Extend Estrogen’s Protective Effects on Memory

Workshop to Examine Optogenetic Approaches for Treating Diseases Associated With Vision Loss Announced

AI Predicts CRISPR’s RNA-Targeting Effects, Revolutionizing Gene Therapy

Activity of Huntington’s Disease Gene Curbed for 6 Months: Mouse Study

Getting Gene Therapy to the Brain

Gene Therapy Restores Walking After Paralysis

Gene Therapy Shows Promise in Treating Neuropathy From Spinal Cord Injuries

Gene Therapy for Completely Color Blind Children Partly Restores Cone Function

Gene Therapy Proven to Shield Brain from TDP-43 Damage

How Severe Illness During Pregnancy Alters Fetal Brain Development

Aging Brains Maintain Robust Language Networks Despite Cognitive Decline

Youth Protein TIMP2 Restores Immune Function in the Aging Brain

Shame, Stigma, and Culture Prevent Male Domestic Violence Survivors From Seeking Help

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