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gene therapy

Featured Genetics Neuroscience Visual Neuroscience

·August 25, 2022·3 min read

New Gene Therapy Shows Promise for Treating Age Related Macular Degeneration

A new study reports that a new gene therapy shows promise in treating dry age-related macular degeneration. The gene therapy, ophNdi1, directly targets mitochondrial function that is malfunctioning in AMD.

Featured Genetics Neuroscience Visual Neuroscience

·August 23, 2022·4 min read

Gene Therapy for Completely Color Blind Children Partly Restores Cone Function

Researchers partially restored the function of cone receptors in the retinas of children born completely blind by using gene therapy.

Featured Genetics Neurology Neuroscience

·May 9, 2022·4 min read

Gene Therapy Shows Promise in Treating Neuropathy From Spinal Cord Injuries

Gene therapy that inhibits targeted nerve cell signals effectively improves symptoms of neuropathic pain without negative side effects in mouse models of spinal cord injury or peripheral nerve damage.

Autism Featured Genetics Neuroscience Open Neuroscience Articles

·May 2, 2022·5 min read

Gene Therapy Reverses Effects of Autism-Linked Mutation in Brain Organoids

A brain organoid study reveals how a genetic mutation associated with Pitt-Hopkins syndrome, a profound form of autism, disrupts neural development. Using gene-editing technology, researchers recovered the function of the TCF4 gene and effectively restored neural structure and function.

Featured Neuroscience Open Neuroscience Articles

·February 9, 2022·5 min read

Astrocytes Display Unique Activity Patterns

Astrocytes may play a significant role in information processing and memory, a new study reports.

Featured Genetics Neurology Neuroscience Open Neuroscience Articles

·May 4, 2021·4 min read

Gene Therapy in Alzheimer’s Disease Mouse Model Preserves Learning and Memory

Novel gene therapy treatment prevents learning impairments and memory loss in mouse models of Alzheimer's disease.

Featured Genetics Neurology Open Neuroscience Articles

·March 19, 2021·3 min read

Gene Therapy Using ‘Zinc Fingers’ May Help Treat Alzheimer’s Disease

A new genetic engineering strategy significantly reduces levels of tau in animal models of Alzheimer's disease. The treatment, which involves a single injection, appears to have long-last effects.

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Featured Genetics Neurology

·February 19, 2021·4 min read

First-in-Human Clinical Trial to Assess Gene Therapy for Alzheimer’s Disease

Researchers launch the first-in-human phase 1 clinical trial to assess the safety and efficacy of a gene therapy which will deliver BDNF to the brains of those with Alzheimer's and mild cognitive impairment.

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Brain Cancer Featured Genetics Open Neuroscience Articles

·August 17, 2020·2 min read

Gene Targeting Helps Overcome the Resistance of Brain Cancer to Therapy

Mouse study reveals the deletion of the OSMR gene significantly improves glioblastoma tumor response to therapy and extended lifespan.

Featured Neurology Neuroscience Videos

·July 30, 2020·4 min read

New Hope as Dementia Therapy Reverses Memory Loss

Activating p38gamma, a naturally protective enzyme in the brain, may help to prevent the development of Alzheimer's disease symptoms. Researchers showed the naturally protective effects of p38gamma could be harnessed to improve memory in the later stages of Alzheimer's disease.

Featured Genetics Neurology

·July 29, 2020·6 min read

Getting Gene Therapy to the Brain

Researchers successfully applied a gene therapy platform to completely correct brain defects in a large animal model of a human genetic disease.

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Featured Genetics Neuroscience Open Neuroscience Articles Visual Neuroscience

·May 1, 2020·5 min read

New gene therapy for complete color blindness tested in patients

New gene therapy may help those with achromatopsia, or complete color blindness, to improve visual function. The treatment targets the CNGA3 gene, which is implicated in one-third of achromatopsia cases.