Gene therapy enables a striking recovery of night vision in those who suffer from the childhood-onset blindness disorder Leber Congenital Amaurosis.
Administering a chemical compound called synthetic retinoids to the retina helped restore brain networks associated with vision and prompted the growth of two times more neurons, effectively restoring vision in adult mouse models of the genetic visual disorder LCA.
Researchers find evidence that a sight restoring gene therapy strengthens visual pathways in the brain.
In three adults, repeat dose safely improves vision. Gene therapy for congenital blindness has taken another step forward, as researchers...