Gene Therapy Researchers Find Viral Barcode to Cross the Blood-Brain Barrier
Researchers have identified structural 'footprints' that allow certain virus vectors reach the brain easily.... Read More...
AAV
First Step Toward CRISPR Cure For ALS
UC Berkeley researchers report they have successfully used CRISPR-Cas9 gene editing to delay symptoms and extend lifespan in mouse models of ALS.... Read More...
Gene Editing in the Brain Gets A Major Upgrade
Max Planck researchers announce they have developed a new tool that can assist with precise genome editing in neurons.... Read More...
Gene Immunotherapy Protects Against Multiple Sclerosis: Mouse Study
A new study in Molecular Therapy reveals gene immunotherapy is able to reverse symptoms of Multiple Sclerosis, and even prevent the disease from appearing in mice.... Read More...
Shining Light on Brain Cells That Coordinate Movement
Researchers have developed a novel technique that allows them to insert a gene into Perkinje cells in the adult brain. This approach, researchers say, could be used to change behavior and alter the function of brain circuits.... Read More...
Gene Therapy Restores Hearing in Deaf Mice…Down to a Whisper
Researchers use gene therapy to help restore hearing in mice down to the equivalent of being able to hear a whisper.... Read More...
New Gene Delivery Therapy Restores Partial Hearing and Balance in Deaf Mice
Summary: Treatment allows mice who would normally be completely deaf to hear the equivalent of a loud conversation, researchers say.Source: Harvard.Usin... Read More...
Delivering Genes Across the Blood-Brain Barrier
A new study reports researchers have successfully modified a virus to be able to enter a mouse brain via the bloodstream and deliver genes to central nervous system cells.... Read More...
Joining Molecular Components Expands Ability to Manipulate Genes in Specific Cell Types
Researchers combine molecular components to manipulate genes in specific cell types.... Read More...