Researchers have identified structural 'footprints' that allow certain virus vectors reach the brain easily.
A new study in Molecular Therapy reveals gene immunotherapy is able to reverse symptoms of Multiple Sclerosis, and even prevent the disease from appearing in mice.
Researchers have developed a novel technique that allows them to insert a gene into Perkinje cells in the adult brain. This approach, researchers say, could be used to change behavior and alter the function of brain circuits.
Summary: Treatment allows mice who would normally be completely deaf to hear the equivalent of a loud conversation, researchers say....
Researchers combine molecular components to manipulate genes in specific cell types.