Researchers have identified structural 'footprints' that allow certain virus vectors reach the brain easily.
UC Berkeley researchers report they have successfully used CRISPR-Cas9 gene editing to delay symptoms and extend lifespan in mouse models of ALS.
Max Planck researchers announce they have developed a new tool that can assist with precise genome editing in neurons.
A new study in Molecular Therapy reveals gene immunotherapy is able to reverse symptoms of Multiple Sclerosis, and even prevent the disease from appearing in mice.
Researchers have developed a novel technique that allows them to insert a gene into Perkinje cells in the adult brain. This approach, researchers say, could be used to change behavior and alter the function of brain circuits.
Researchers use gene therapy to help restore hearing in mice down to the equivalent of being able to hear a whisper.
Summary: Treatment allows mice who would normally be completely deaf to hear the equivalent of a loud conversation, researchers say....
A new study reports researchers have successfully modified a virus to be able to enter a mouse brain via the bloodstream and deliver genes to central nervous system cells.
Researchers combine molecular components to manipulate genes in specific cell types.
