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gene therapy

This shows a doctor looking at brain scans

Brain Cancer Featured Genetics Open Neuroscience Articles

·August 17, 2020·2 min read

Gene Targeting Helps Overcome the Resistance of Brain Cancer to Therapy

Mouse study reveals the deletion of the OSMR gene significantly improves glioblastoma tumor response to therapy and extended lifespan.

Featured Genetics

·December 9, 2015·4 min read

Gene Therapy Could Extend Estrogen’s Protective Effects on Memory

Researchers use gene therapy to help extend the effectiveness of estrogen for retaining memory.

Featured Genetics

·November 15, 2015·6 min read

Gene Therapy For Brain Disorders Delivered by Eye Drops

Researchers have developed a simplified approach for delivering and monitoring gene therapy for brain disorders.

Featured Genetics Neuroscience Visual Neuroscience

·August 23, 2022·4 min read

Gene Therapy for Completely Color Blind Children Partly Restores Cone Function

Researchers partially restored the function of cone receptors in the retinas of children born completely blind by using gene therapy.

Featured Genetics Neuroscience Visual Neuroscience

·April 26, 2023·3 min read

Gene Therapy for Dogs With Inherited Blinding Eye Disease Set for Human Trials

A groundbreaking gene therapy proven successful in treating an inherited, blinding eye disease in dogs is now poised for clinical trials in humans with the rare condition retinitis pigmentosa. The therapy, which halts vision loss by introducing a normal copy of the CNGB1 gene, could potentially benefit around 2 million people affected worldwide.

Featured Genetics Neurology

·February 8, 2012·4 min read

Gene Therapy for Inherited Blindness Succeeds in Patients’ Other Eye

In three adults, repeat dose safely improves vision. Gene therapy for congenital blindness has taken another step forward, as researchers...

Featured Genetics Neurology Neuroscience Open Neuroscience Articles

·May 4, 2021·4 min read

Gene Therapy in Alzheimer’s Disease Mouse Model Preserves Learning and Memory

Novel gene therapy treatment prevents learning impairments and memory loss in mouse models of Alzheimer's disease.

Featured Genetics Neurology Neuroscience Open Neuroscience Articles

·January 19, 2019·3 min read

Gene Therapy Promotes Nerve Regeneration

A new study reveals gene therapy in combination with neurosurgery can help to improve the rate of survival and promote regeneration of nerve fibers.

Featured Genetics Neurology Neuroscience

·May 26, 2026·10 min read

Gene Therapy Proven to Shield Brain from TDP-43 Damage

An experimental gene therapy called SynCav1 can protect the central nervous system from the cognitive decline linked to TDP-43-related proteinopathy, a primary driver of FTD, ALS, and over half of all Alzheimer’s cases.

Featured Genetics Neuroscience Open Neuroscience Articles Visual Neuroscience

·October 10, 2022·4 min read

Gene Therapy Rapidly Improves Night Vision in Adults With Congenital Blindness

Gene therapy enables a striking recovery of night vision in those who suffer from the childhood-onset blindness disorder Leber Congenital Amaurosis.

Auditory Neuroscience Featured Genetics Neuroscience

·July 3, 2025·5 min read

Gene Therapy Restores Hearing in Those with Deafness

A new study shows that gene therapy can significantly improve hearing in both children and adults with congenital deafness caused by mutations in the OTOF gene. The therapy uses a synthetic virus to deliver a healthy copy of the gene directly to the inner ear, with hearing improvements observed in all ten participants within one month.

Featured Genetics Neuroscience Visual Neuroscience

·September 6, 2024·4 min read

Gene Therapy Restores Vision

A new gene therapy has restored vision in patients with Leber congenital amaurosis type I (LCA1), a rare genetic condition causing blindness. In a small trial, those receiving the highest dose saw up to a 10,000-fold improvement in light sensitivity and significant gains in reading and navigation abilities.

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gene therapy

Gene Targeting Helps Overcome the Resistance of Brain Cancer to Therapy

Gene Therapy Could Extend Estrogen’s Protective Effects on Memory

Gene Therapy For Brain Disorders Delivered by Eye Drops

Gene Therapy for Completely Color Blind Children Partly Restores Cone Function

Gene Therapy for Dogs With Inherited Blinding Eye Disease Set for Human Trials

Gene Therapy for Inherited Blindness Succeeds in Patients’ Other Eye

Gene Therapy in Alzheimer’s Disease Mouse Model Preserves Learning and Memory

Gene Therapy Promotes Nerve Regeneration

Gene Therapy Proven to Shield Brain from TDP-43 Damage

Gene Therapy Rapidly Improves Night Vision in Adults With Congenital Blindness

Gene Therapy Restores Hearing in Those with Deafness

Gene Therapy Restores Vision

PCOS/PMOS Increases Alzheimer’s Risk

Alcohol Tricks Brain Cells Into Destroying Themselves

Daytime Napping Linked to Higher Risk of Dementia

Prenatal Stress Alters the Placenta to Shape Fetal Brain Development

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