FeaturedGeneticsNeurology·June 27, 2012·3 min readNew Compound Holds Promise for Treating Duchenne MD and Other Inherited DiseasesRTC 13 effectively counteracts ‘nonsense’ mutation that causes disorder. Scientists at UCLA have identified a new compound that could treat...Read More
FeaturedNeurology·January 22, 2013·4 min readDiscovering the “Needle in a Haystack” for Muscular Dystrophy PatientsScientists identified a sequence in the dystrophin gene that is essential for helping muscle tissues function, a breakthrough discovery that could lead to treatments for the deadly hereditary disease.Read More
FeaturedGenetics·February 7, 2013·5 min readExperimental Gene Therapy Treatment for Duchenne Muscular Dystrophy offers Hope for YoungsterA nationwide clinical trial for a new type treatment that could offer help to those suffering from Duchenne Muscular Dystrophy, a devastating neuromuscular disease.Read More
FeaturedGeneticsOpen Neuroscience Articles·June 4, 2013·3 min readGenetic Editing for Duchenne Muscular DystrophyResearchers have been able to repair a defect responsible for Duchenne muscular dystrophy by using a novel genetic editing technique.Read More
FeaturedNeurology·August 1, 2013·5 min readBurnt Sugar-Derivative Reduces Muscle Wasting in Fly and Mouse Models of Muscular DystrophyMuscle regeneration in mouse models of Duchenne muscular dystrophy is improved when THI is purified and given in appropriate doses, a new study suggests.Read More
FeaturedNeurology·March 26, 2014·4 min readHistory Is Made with First Small LVAD Implant for Young PatientA patient with Duchenne muscular dystrophy is only one of three people in the US to receive a LVAD to keep his weakened heart pumping blood around his body.Read More
FeaturedNeuroscienceNeuroscience VideosOpen Neuroscience Articles·January 13, 2015·4 min readFirst Contracting Human Muscle Grown in LaboratoryResearchers report they have created the first lab grown, contracting human muscles.Read More
FeaturedGenetics·February 13, 2016·6 min readDuchenne Muscular Dystrophy Could Be Helped By Stem Cell Gene TherapyA newly developed approach could be used to treat Duchenne muscular dystrophy, researchers believe.Read More
FeaturedGeneticsNeurologyOpen Neuroscience Articles·June 28, 2016·3 min readNew Method to Grow and Transplant Muscle Stem Cells Holds Promise for Treatment of MDA new study reports on a new method of stem cell transplantation that could help people with Duchenne muscular dystrophy.Read More
FeaturedNeurology·September 19, 2016·4 min readFirst Drug to Treat Duchenne Muscular Dystrophy Approved by FDAThe FDA have approved the first drug designed to treat patients with Duchenne muscular dystrophy.Read More
FeaturedGeneticsNeurology·October 13, 2016·4 min readIncreasing Understanding of Duchenne Muscular DystrophyA new study may help to increase understanding of Duchenne muscular dystrophy.Read More
FeaturedGeneticsNeurologyOpen Neuroscience Articles·April 13, 2017·4 min readCRISPR Corrects Duchenne Muscular DystrophyResearchers successfully use CRISPR-Cpf1 to correct Duchenne muscular dystrophy in both animal and human cells.Read More
