Researchers successfully use CRISPR-Cpf1 to correct Duchenne muscular dystrophy in both animal and human cells.
Scientists identified a sequence in the dystrophin gene that is essential for helping muscle tissues function, a breakthrough discovery that could lead to treatments for the deadly hereditary disease.
A newly developed approach could be used to treat Duchenne muscular dystrophy, researchers believe.
The FDA have approved the first drug designed to treat patients with Duchenne muscular dystrophy.
A new study may help to increase understanding of Duchenne muscular dystrophy.
Researchers report muscle stem cells may give rise to rhabdomyosarcoma, a rare cancer that affects the muscles in Duchenne muscular dystrophy. The study also identifies two genes linked to the tumor's growth.
RTC 13 effectively counteracts ‘nonsense’ mutation that causes disorder. Scientists at UCLA have identified a new compound that could treat...
Researchers from Cardiff University are working in conjunction with biotech company PerkinElmer, to develop a new diagnostic kit of Duchenne muscular dystrophy. The kit will be able to screen for DMD by analyzing dried neonatal blood spots.
Shortened telomeres may impede the ability for new muscle regeneration in those with Duchenne Muscular Dystrophy, a new study reports.
